2021 International LGMD Conference - Day 3 (from Sunday, September 19, 2021)

This video features all the programming from the third day of our 2021 International LGMD Conference, a program of The Speak Foundation. On this day, you can find: (1) “Sponsored Session: Ask Bio” with Anh Nguyen, MD (AskBio, USA), Nicholas E. Johnson, MD (Virginia Commonwealth University, USA), Craig Norton (USA), CJ Norton (USA), and Sharon Hesterlee, PhD (Muscular Dystrophy Association, USA) – In this 90-minute presentation, AskBio introduces and gives an overview of their patient advocacy program and presents the pre-clinical data supporting the clinical advancement of LION-101. They also offer an inside look from a GRASP LGMD Investigator into gene therapy trials, and into the perspectives and challenges of living with LGMD2i from a patient family. (2) “My LGMD Story“ with the Szymczak Family (USA). (3) “My LGMD Story“ with Andrew Robertson (UK). (4) “Diagnostic Landscape for LGMDs” with Moderator Laura Rufibach, PhD (Jain Foundation, USA), Jorge Bevilacqua, MD, PhD (University of Chile, Chile), Conrad (Chris) Weihl, MD, PhD (Washington University School of Medicine, USA), Monkol Lek, PhD (Yale University School of Medicine, USA), Mark Barnett (USA), Kyle Harrington (USA), Jenna Keindel (Canada), Andrea Klein (USA), and Noni Uribe (USA) – Currently diagnosing LGMDs and other conditions causing similar symptoms is often challenging. Clinicians and geneticists describe the diagnostic process, with patients sharing their journeys. For more information about the International LGMD Conference, please visit our conference website at . We want to thank our platinum sponsors of the 2021 International LGMD Conference: Sarepta Therapeutics, AskBio, and GFB Onlus. The International LGMD Conference is a program of The Speak Foundation, a 501(c)(3) nonprofit charity and the first patient-led organization for muscular dystrophy. If you would like to donate to the life-saving mission of The Speak Foundation, please go to